Data presented at the 2026 Muscular Dystrophy Association meeting could have readthroughs to companies developing therapies for spinal muscular atrophy, Duchenne muscular dystrophy and Becker muscular ...
Genethon, a pioneer and leader in gene therapy for rare diseases, unveiled results at the MDA Conference in Orlando confirming the long-term efficacy of its GNT0004 gene therapy in Duchenne muscular ...
Annie Wilson learned to edit videos of adoptable dogs with her eyes because of her deep love for senior dogs at Muttville ...
Paul Wilson stashed an 'arsenal' of firearms in his bungalow after finding himself 'in a situation he couldn't get out of' ...
New Phase 1b data support the safety and effectiveness of salanersen over one year in children with SMA who had the potential for improvement due to suboptimal clinical status with prior gene ...
Biogen’s salanersen is now heading into three Phase III trials in SMA.
US biotech major Biogen has presented additional results from the Phase Ib study of salanersen, an investigational novel antisense oligonucleotide (ASO) given once a year for spinal muscular atrophy ...
The Society for the Education of the Challenged (SEC) has been left anxious after receiving a notification from the state’s Welfare of Disabled Department directing the institution to shift its ...
Barclays 28th Annual Global Healthcare Conference March 11, 2026 8:00 AM EDTCompany ParticipantsMatthew Klein - CEO ...
The pharmaceutical and biotech sectors have seen a flurry of executive movement this month, with leadership changes spanning global giants, clinical-stage biotechs, and specialist pharma companies ...
The Electric Wheelchair Market has witnessed significant growth in recent years due to the rising demand for advanced ...