New treatments for neurodegenerative diseases like Alzheimer's, Parkinson's, and motor neuron disease (MND) could be unlocked ...
FDA approves Wellcovorin for ultra-rare disease. The Trump admin touted it as a treatment for autism
The Food and Drug Administration (FDA) on Tuesday granted expanded approval to Wellcovorin for the ultra-rare disease cerebral folate deficiency (CFD) in both children and adults, the same ...
A well-fitted ‘disguise’ allows transplanted mitochondria to slip into cells whose own mitochondria are defective, scientists ...
A team from the University of Barcelona has designed and validated in animal models an innovative compound with a pioneering ...
Melissa Claire Egan, known for her roles in daytime soap operas "The Young and the Restless" and "All My Children," revealed she was diagnosed with coronary heart disease in late January. The actress, ...
Life-saving treatments for children with orphan illnesses often move slowly, if at all, through the federal approval process.
Indiana University School of Medicine scientists have uncovered new evidence that an age-related blood condition may contribute to inflammatory bowel disease (IBD). Their findings suggest that a new ...
The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments addressing ultrarare diseases. The FDA unveiled draft guidance on a proposed ...
Iran sends first significant message of de-escalation, but with a major caveat Alabama set to execute man who did not kill anyone Daryl Hannah blasts 'Love Story,' calls show 'tragedy-exploiting' IRS ...
Lizzy Lawrence leads STAT’s coverage of the Food and Drug Administration. She was previously a medical devices reporter. You can reach Lizzy on Signal at lizzylaw.53. John Wilkerson is a Washington ...
Artificial intelligence is inventing new drugs against Parkinson's disease, antibiotic-resistant superbugs and many rare diseases – progress that many scientists never dreamed possible. For around ...
It’s possible to achieve remission if you have Crohn’s disease, but it isn’t always easy to find a treatment that will help you get there. Many people with inflammatory bowel disease (IBD) switch ...
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