LOS ANGELES (KABC) -- It's been more than a month since the FDA approved two milestone gene-editing treatments for sickle cell disease, but lining up patients for these therapies will be a challenge ...
Exa-cel, a new CRISPR-based treatment, modifies the genes of the patient's stem cells to induce them to produce fetal hemoglobin. I have a long-standing interest in sickle cell anemia, a genetic ...
Both new FDA-approved medicines offer a potential cure, but they will come with a hefty price tag and it will be years before their long-term effects are clear. Sickle cell disease, a painful ...
In the ever-evolving realm of modern medicine, a once-distant dream to conquer disease through genetics has now inched closer to reality. Last Friday, the U.S. Food and Drug Administration approved ...
Sickle cell anemia is the most severe form of sickle cell disease (SCD). Treatments for sickle cell anemia include medications, blood transfusions, and bone marrow transplants. SCD is a group of ...
Federal officials Friday approved two gene therapy treatments for sickle cell disease, welcome news for thousands with the inherited blood disorder that causes terrible pain crises and early death.
He's the first in New York to receive the novel treatment and one of the first in the world. Share on Facebook (opens in a new window) Share on X (opens in a new window) Share on Reddit (opens in a ...
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Sickle Cell Anemia Symptoms

Sickle cell anemia refers to a group of genetic blood disorders that affect a person’s levels of hemoglobin, the protein in ...
Share on Pinterest World-first genetic therapy approved in the U.K. may be a game changer in sickle cell disease treatment. Image credit: Louise Morgan/Getty Images. As of 2021, almost 8 million ...
Sickle cell anemia causes sickle-shaped cells to block blood flow to the lungs, leading to acute chest syndrome. Common treatment methods involve oxygen supplementation and pain management. Sickle ...
A parasite that causes malaria is halted by sickle cells and makes people who carry the sickle cell trait more resistant to the disease. This is why sickle cell trait also occurs more in people who ...