Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative ...

A team of researchers has developed a promising new approach to detecting neuromuscular disorders using intramuscular electromyography (iEMG). In a pilot study, the automatic diagnostic system showed ...

Kids and teenagers with spinal muscular atrophy had more mobility after receiving a single-dose gene replacement therapy, ...

FDA Approves Treatment for gMG FDA Approves Amgen’s UPLIZNA® (inebilizumab-cdon) for Generalized Myasthenia Gravis (gMG), ...

The rare disorder Kennedy’s disease leads to progressively worsening muscle weakness in the limbs as well as difficulty speaking and swallowing. There are no FDA-approved treatments for the inherited ...

—Children with neuromuscular diseases and cerebral palsy often report disrupted sleep, which is usually attributed to breathing disorders. But new research points to a new potential contributor: ...

(Reuters) - Stealth BioTherapeutics Corp's shares crashed on Friday after its lead neuromuscular disorder drug candidate failed to help patients walk better and reduce fatigue, a major setback to the ...

In a study published in the New England Journal of Medicine, Delp, a professor of bioengineering, and his collaborators ...

Soraya Bekkali, Alexion SVP Europe, Canada and International region, discusses the realities patients with generalised Myasthenia Gravis face across Europe, and how modernised, evidence-based care ...

Using two smartphone cameras and a free video app, a detailed intervention can be produced with accuracy for diagnosing neuromuscular diseases. The innovative discovery was made by researchers from ...

This year marks the tenth anniversary of the TREAT-NMD Advisory Committee for Therapeutics (TACT), a group of multidisciplinary experts that evaluates drug development programmes for rare ...

The Muscular Dystrophy Association (MDA) recognizes the U.S. Food and Drug Administration (FDA) approval of Amgen's UPLIZNA(R) (inebilizumab-cdon) for the treatment of generalized myasthenia gravis ...